Clinical Trials · NCT05168774
FRDA Investigator Initiated Study (IIS) With Elamipretide
- Phase
- Phase 1/Phase 2
- Recruitment status
- Completed
- Sponsor
- Children's Hospital of Philadelphia
- Enrollment
- 20
- Start date
- Mar 2022
- Locations
- 1 site, United States
- Primary endpoint
- Change in High Contrast Visual Acuity